Hematopoietic Stem-Cell Gene Therapy for Cerebral Adrenoleukodystrophy
Hello Project Heartbeat folks! Check out this study from the New England Journal of Medicine about the effects of Lenti-D gene therapy as a safe and effective solution to cerebral adrenoleukodystrophy: Hematopoietic Stem-Cell Gene Therapy for Cerebral Adrenoleukodystrophy Article








